The Chosun Ilbo on MSN
British boy walks, swims post-SMA gene therapy
A 5-year-old British boy with the rare disease spinal muscular atrophy (SMA) has miraculously learned to walk four years after receiving the world’s most expensive gene therapy. On the 31st, the BBC ...
FRESNO Calif. (KFSN) -- The living room of Zaira De La Cruz's home has been turned into a makeshift hospital room. About seven months after her daughter was born, Zoey was diagnosed with the James ...
THAT ARE RIGHT THERE ON YOUR SCREEN. TONIGHT. A REASSURING UPDATE FOR A FAMILY OF TWIN BOYS. WE BROUGHT YOU THIS STORY ON MONDAY. THE BOY WAS BORN WITH A RARE ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
—In a retrospective analysis, a U.S.-based team of experts recently reported that health-related quality of life (HRQoL) after surgery for early-onset scoliosis (EOS) varies significantly depending on ...
New Evrysdi five-year data from the SUNFISH study showed continued stabilisation of motor function in a broad population of individuals with Types 2 or 3 spinal muscular atrophy (SMA) Late-breaking ...
Biogen Inc. announced positive interim results from a Phase 1 study of salanersen (BIIB115/ION306), a novel antisense oligonucleotide for treating spinal muscular atrophy (SMA). The data show that ...
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