A domestically developed gene-editing therapy has successfully treated patients with beta-thalassemia, allowing them to live without the need for lifelong blood transfusions, according to a study ...

Scientists are laying the groundwork for treating one of the most common genetic conditions in humans. Research out today ...

NIH-funded UT team and colleagues from Metagenomi Thereapeutics discovered highly efficient enzyme could enable targeted gene editing within the human body.

So far, clinical applications of CRISPR-based gene editing have been largely limited to editing a person's cells outside of their body and then ...

A new pill could be the future of treatment late-stage pancreatic cancer in the U.S., nearly doubling the length patients ...

At AACR 2026, the Genialis™ Supermodel–powered RNA survival model outperforms standard of care in real-world clinical data, establishing a scalable biomarker framework for ADC drug developmentBOSTON-- ...

Every year, sepsis kills roughly 11 million people worldwide, more than lung cancer and heart attacks combined. Despite ...

The ACC has published a scientific statement regarding the use of gene editing therapy for cardiovascular disease.

A research team has discovered an enhanced CRISPR gene-editing system that could enable targeted delivery inside the human ...

Monday’s FDA approval makes Filspari the first therapy specifically indicated for FSGS, a condition that represents a $1 ...

Prostate cancer is one of the most prevalent malignancies in men and remains a leading cause of cancer-related morbidity and mortality worldwide. For many, prostate cancer follows an indolent course, ...