CRISPR Cas9 gene therapy explained with DNA scissors, hereditary diseases treatment, and designer babies ethical dilemmas ...

A phase 1/2 trial of a novel viral vector gene therapy in adults with type 1 diabetes is scheduled to begin this year.

Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.

UF scientist develops safer gene therapy restoring vision in children with rare inherited eye diseases; pivotal trials begin ...

Durable expression of anti-sickling fetal hemoglobin and reduction in sickle hemoglobin ob ...

Technologies for the development of new RNA treatments and gene therapy are marking new milestones in Italy, with the ...

Add Yahoo as a preferred source to see more of our stories on Google. The US Food and Drug Administration (FDA) has approved Rocket Pharmaceuticals’ Kresladi (marnetegragene autotemcel) in leukocyte ...

All five patients in the trial received CS-101, a treatment developed by Chinese researchers, and achieved fast hematopoietic reconstruction. This process allows the body to restart its blood-making ...

Scientists are laying the groundwork for treating one of the most common genetic conditions in humans. Research out today ...

NIH-funded UT team and colleagues from Metagenomi Thereapeutics discovered highly efficient enzyme could enable targeted gene editing within the human body.

The IOC's ban on trans women in female sports raises fairness concerns amid growing discrimination and questions about ...

A mother's persistence helps revive an all-but-abandoned drug class and could aid her son and thousands of others with ...